The Wave 1 gene therapy trial involves the CF gene delivered by liposomes. Trial dosing is likely to finish around June, with results hopefully announced in October.
The Wave 2 product appears to be a more effective form of gene therapy. This involves a CF gene delivered by a virus. Trials will hopefully start early 2017.
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CFTR Modulators currently help multiple organs by increasing the function of the CFTR protein.
Gene Therapy helps the lungs with a less frequent medication, but is further behind in terms of trial development.
In the future could gene therapy be used in conjunction with CFTR modulators?